Genetic Disease Research appeal
From rare conditions like COL4A1 to hearing loss and inherited dementia. With your help, the University of Sheffield will use gene therapies to save lives and rewrite futures.
Thank you
![Group of Big Walk participants wearing orange t shirts and walking in a line through countryside](http://cdn.sheffield.ac.uk/sites/default/files/styles/mobile_single_column_1x/public/2022-07/DSC06080.jpg?itok=Ap44GYZP&h=376b0cc8)
You're bringing hope to so many people
Thanks to the support of almost 5,000 donors so far, Sheffield researchers are getting one step closer to creating new treatments for genetic diseases.
Follow the progress of the GTIMCCould you help the team do even more?
Who you'll help
A proven treatment for genetic diseases
![Babies Grace and Sebastian smiling at the camera](http://cdn.sheffield.ac.uk/sites/default/files/styles/mobile_single_column_1x/public/2022-03/GIV - SMA BABIES.png.jpg?itok=4ok-tQib)
Genetic disease research is already saving lives
The team behind Sheffield's gene therapy research has already shown it works. Thanks to a revolutionary new treatment, babies with Spinal Muscular Atrophy now have full futures ahead of them.
Discover the potential of gene therapy